Spinal muscular atrophy is a rare genetic disorder that frequently leads to early death in kids. However, an experimental drug provided incredible results in a new trial. This drug even enabled several children with the condition to walk again.
The results of the drug, nusinersen, were so incredible that the trial was cut short in August, as it was unfair and to keep some of kids on placebo.
Scientists believe if the final results of the trial will prove the drug efficiency, they could offer hope for patients with similar conditions, such as Hunrigton’s disease, motor neurone disease, and Alzheimer’s disease.
More information about the trial here.